Qure shares finished the regular trading week down only 9% despite the FDA’s hard-line stance and public criticism against the company’s Huntington’s disease (HD) gene therapy candidate AMT-130.

Using rodent and cellular models, the researchers showed that tanycytes take up tau from the CSF and release it into ...

The CNBC Cures Summit, held in New York earlier this week, opened with a simple but urgent premise: every step forward changes someone’s life.

The new center offers immersive, hands-on access to advanced cryo-EM technologies designed to accelerate structural insights.

A single treatment of viral vector-delivered CAR-A construct in mice with existing plaque saturation cut the amount of amyloid plaques in half.

From analytical control through downstream processes to manufacturing, BsAbs present challenges in protein expression, purity, and stability.

Ongoing research aims to confirm the mechanism by which ICP4 fluidizes the nucleus, which could indicate specific targets to counter viral replication.

Researchers say study findings have highlighted biomarkers that could help improve early diagnosis of esophageal cancer, when it is easier to treat.

Progeria, an ultrarare and fatal genetic disease characterized by rapid aging, can affect children and young adults.

Researchers hope to undertake clinical studies in multiple cancers, including ovarian cancer, glioblastoma, and others.

Researchers at Sanofi report that cas-CLOVER (deactivated Cas9 fused to the C-terminus of Clostridium Clo051) gene editing has the potential to notably enhance recombinant protein production in ...

When the performance of AI models was assessed within stratified patient subgroups, such as only high-grade breast cancers or only MSI-positive tumors, accuracy fell substantially, revealing that the ...