News

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...
Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after ...
After spending over 300 days at CHOP, KJ Muldoon has been released from the hospital after receiving personalized CRISPR gene ...
The world’s first patient to successfully receive a CRISPR gene-editing treatment was discharged from Children’s Hospital of Philadelphia on June 2, ABC News reported.  KJ Muldoon, a 10-month-old who ...
KJ Muldoon's life-threatening disorder, called severe carbamoyl phosphate synthetase 1 (CPS1) deficiency, was treated with ...
KJ Muldoon came into the world with a genetic time bomb ticking inside him. Doctors at the Children’s Hospital of Philadelphia had barely finished running newborn screens when the diagnosis landed: ...
The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.
Scientists sprinted to create personalized medicine for baby KJ powered by CRISPR, a powerful gene-editing technology that won the Nobel Prize five years ago.
A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...
Within minutes of KJ Muldoon’s birth, doctors knew there was something very wrong. Five weeks premature, his little arms went rigid when lifted and shook oddly on the way back down. An attentive ...
05. For the ailing gene editing industry, hope came earlier this month in the tiny, smiling, fuzzy-headed form of KJ Muldoon. At just 6 months old, KJ received a gene-editing treatment custom ...