Intrathecal treatment with a vector-based gene therapy was associated with a greater improvement in motor function at 52 ...

The FDA has accepted for Priority Review the BLA for apitegromab for the improvement of motor function in patients with spinal muscular atrophy.

Our Bureau, New Delhi Thursday, April 3, 2025, 08:00 Hrs [IST] ...

Leader of Opposition Suvendu Adhikari donated Rs 10 lakh from his salary towards the treatment of a girl from West Bengal's ...

Chugai Pharma’s Evrysdi tablets 5mg receives Japanese approval to treat spinal muscular atrophy: Saturday, March 29, 2025, 11:00 Hrs [IST] Chugai Pharmaceutical Co., Ltd. announ ...

“During the wait for the results, things deteriorated. He was choking constantly, not going to the toilet for days and his ...

A film about a Kent boy who lives with a rare condition has been nominated for a Bafta TV award. Sky's Disability & Me ...

Japanese drugmaker Chugai (TYO: 4519) has obtained regulatory approval from the Ministry of Health, Labor and Welfare (MHLW) ...

“We were referred to a paediatrician who put him on reflux medication. However, things were getting worse,” Ellie said. “He ...

A majority of people have supported the urgent implementation of early screening for a genetic disease that causes severe ...

I was one of those strange kids in high school who could write well over the mandatory composition word count in English ...